A member asked:

How might gene therapy be used to treat muscular dystrophy?

A doctor has provided 1 answer
Dr. Felix Brizuela answered

Specializes in Neurology

A lot: Replacing dystrophin, the dysfunctional protein in duchenes and beckers muscular dystrophy involves either replacing the bad gene for the good or copying the right protein from the correct gene and replacing it. Either way, genes are the mainstay of therapy.

Answered 5/16/2013

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