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A member asked:
What disease is gene therapy is used to treat?
2 doctors weighed in across 2 answers
Gene therapy: Treating certain congenital enzyme deficiency metabolic disorders. Looks promising in hemophilia where research going. Also lot of interest in cancers and treating infectious diseases.
Answered 2/22/2013
5.3k views
Selected: Gene therapy describes an approach whereby genetic technology will be used to treat many conditions. The easiest use of gene therapy is to replace a faulty gene. An example is glybera which is approved in europe to treat lipoprotein lipase deficienct, a rare genetic disorder.
Answered 3/10/2013
5.3k views
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