A member asked:

What genetic disorder can be cured by bone marrow transplants?

A doctor has provided 1 answer

Blood related.: A bone marrow transplant gives someone a new immune system, and new cells from which to make red cells, white cells and platelets. Bmt can cure genetic hemoglobin disease like thalassemia major, where a person cannot make red cells. Bmt can cure congenital neutropenias (very low white cells). Immune system defects such as severe combined immune deficiency (scid) are candidates too.

Answered 2/8/2013

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