A member asked:

Are leukodystrophies like metachromatic leukodystrophy (mld) treatable?

A doctor has provided 1 answer

Leukodystrophy: There is no cure for mld. Bone marrow transplantation may delay progression of the disease in some cases. Other treatment is symptomatic and supportive. Considerable progress has been made with regard to gene therapy in an animal model of mld. (http://www.Ninds.Nih.Gov/disorders/metachromatic_leukodystrophy/metachromatic_leukodystrophy.Htm).

Answered 10/29/2012

5.8k views

Thank

Related Questions

A member asked:

What is metachromatic-leukodystrophy? What causes it?

A doctor has provided 1 answer

A member asked:

What is the treatment for leukodystrophy?

A doctor has provided 1 answer

A member asked:

Does leukodystrophy cause extreme tiredness?

2 doctors weighed in across 2 answers

A member asked:

Are there any possible treatments for leukodystrophy?

A doctor has provided 1 answer

A member asked:

What is the life expectancy for patients with leukodystrophy?

A doctor has provided 1 answer