A 42-year-old female asked:
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Please advice about the following therapy for thalassemia purpose- Bluebird Bio Gene Therapy Hydroxyurea Therapy When the therapy will be available?

1 doctor answer
Dr. David Masiello
17 years experience in Hematology and Oncology
Now: Hydroxurea is already available. I believe what you are inquiring about is gene therapy, inserting the normal beta globulin gene into someone with a hemoglobinopathy. This is currently in development and it is unclear when this, if ever, will be available outside a clinical trial.
Answered on Apr 16, 2017
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