A member asked:

Is it possible to cure morguio syndrome?

A doctor has provided 1 answer

No: Morquio's syndrome (referred to as mucopolysaccharidosis IV or morquio's) is an autosomal recessive mucopolysaccharide storage disease (see also lysosomal storage disorder), usually inherited. It is a rare type of birth defect with serious consequences. Because it is genetic, there is no cure, but it can be treated with enzyme replacement therapy.

Answered 6/10/2014

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