A member asked:

What is a successful cure of hemophilia(factor viii deficiency).?

3 doctors weighed in across 2 answers

None: Hemophilia is treated with recombinant factor viii, however, it is not a cure.

Answered 12/29/2013

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None currently: For hemophilia b, however, there are very encouraging results using gene therapy in humans. Hemophilia a (factor viii deficiency) is harder to treat by current gene therapy methods because the gene is huge. There are some gene editing techniques that have shown promise in mouse models. Hopefully soon some of these will make it to clinical trials in humans.

Answered 1/26/2014

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Is it possible to cure hemophilia b?

A doctor has provided 1 answer