How might gene therapy be used to treat muscular dystrophy?

A lot. Replacing dystrophin, the dysfunctional protein in duchenes and beckers muscular dystrophy involves either replacing the bad gene for the good or copying the right protein from the correct gene and replacing it. Either way, genes are the mainstay of therapy.

Related Questions

How might gene therapy be used to treat muscular dystrophies?

In hopes to cure. Gene therapy is targeted at replacing the damaged segments of dna with more normal copies so that the body can produce adequate dystrophin--the protein missing in duchenne. So far no one has found a method that successfully delivers the gene, largely because it is very big. But there is still a lot of work in this area being done. Read more...

How much will gene therapy cost for muscular dystrophy?

Too early to tell. The science and technology is only in its infancy... Probably will be decades before it is a reality. Read more...

What is the genetic inheritance of duchenne muscular dystrophy?

X-linked inheritance. Duchenne muscular dystrophy is caused by a mutation of the dmd gene on the x chromosome. A woman who is a carrier will pass the mutation (on average) to half of her sons and half of her daughters, but only the sons will develop muscular dystrophy - because they have only one x chromosome. Carrier females with one normal dmd gene are usually free of symptoms. Your genetic counselor can explain more. Read more...
X linked. The gene for the abnormal protein is located on the x chromosome. Hence it is "x linked" . Mostly boys are affected. Read more...

What type of genetic disorder is the duchenne muscular dystrophy?

"X-Linked recessive" This means that the problem causing this disease is carried on the x chromosome. Women have 2 of these, men just one. If a boy has an x chromosome that has this genetic defect, there is no other dna to "cover" this up and that boy will have the disease. Women have 2 copies of dna, and only can be carriers. Mothers can then pass this problem on to their sons, however. Read more...

How come duchenne muscular dystrophy considered a genetic disorder?

Mutated gene in X . Duchenne muscular dystrophy is caused by an abnormal gene in x chromosome, and is inherited as an x-linked recessive trait. Read more...
Its chromosomal. The gene for the abnormal protein is located on the x chromosome. Hence it is "x linked" . Mostly boys are affected. Read more...

How do gene defects cause different forms of muscular dystrophy?  

Coding. Like the order of letters in a word can spell and mean something different, so too can the order and type of genes cause a particular disease presentation. When someone has genes for muscular dystrophy, it depends on how strong those genes are and what they code for that determines what form of dystrophy they will have. Read more...
Long answer . We are limited to 400 characters, so i can't go into a lot of detail. Duchenne muscular dystrophy is caused by the failure of the body to make dystrophin. Beckers dystrophy has more dystrophin, but not nearly as much as normal. There are other genetic defects that i don't have enough room to go into further detail. Try www.Aaos.Org or another reputable site. Read more...

Can exon skipping or stem cell therapy helpful in duchccne muscular dystrophy?

Perhaps in future. Unfortunately, not available yet, but muscular dystrophy association is well financed thanks to jerry lewis, and research is advancing steadily. Stay tuned. Read more...

Does being diagnosed with Myotonia through genetic testing of the Scn4a gene mean a person has Myotonic Muscular Dystrophy? Is Myotonia a Dystrophy?

Usually. Myotonia, can have more than one cause. Myotonic dystrophy, is a genetics, and heritage form of Maya Tonio. If you have the gene, you most likely have it. Myotonia is due to an abnormality in the membranes of muscle cells, making them hyperexcitable. Read more...

How does the dystrophin gene which causes becker type muscular dystrophy get mutated?

Many. Gene can mutate due to many destructive processes lik radiation, chemicals or trauma as well as vitamin/mineral issus and metabolic disorders. Read more...
2 ways. Genetic information is passed down from parents to their child, either accurately, or with random changes called "spontaneous" mutations. Muscular dystrophy can be inheirited, or occur for the first time in an individual. The actual number of dystrophin "copies" made by the gene of the individual can vary. Environmental factors are not suspected at this time. Read more...