2 doctors weighed in:
How might gene therapy be used to treat muscular dystrophy?
2 doctors weighed in

Dr. Felix Brizuela
Neurology
1 doctor agrees
In brief: A lot
Replacing dystrophin, the dysfunctional protein in duchenes and beckers muscular dystrophy involves either replacing the bad gene for the good or copying the right protein from the correct gene and replacing it.
Either way, genes are the mainstay of therapy.

In brief: A lot
Replacing dystrophin, the dysfunctional protein in duchenes and beckers muscular dystrophy involves either replacing the bad gene for the good or copying the right protein from the correct gene and replacing it.
Either way, genes are the mainstay of therapy.
Dr. Felix Brizuela
Dr. Felix Brizuela
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