2 doctors weighed in:

Are there different options for treating mucolipidoses?

2 doctors weighed in
Dr. Michael Ekizian
Internal Medicine
1 doctor agrees

In brief: Inborn errors

Complications of the mucopolysaccharidoses (mps) can be widespread, affecting the respiratory, cardiac, skeletal and connective tissue, and nervous systems.
Most treatments for mps are symptomatic and cannot prevent the eventual decline in function. However, specific therapies, such as hematopoietic stem cell transplantation or enzyme replacement, may alter the natural history of these diseases.

In brief: Inborn errors

Complications of the mucopolysaccharidoses (mps) can be widespread, affecting the respiratory, cardiac, skeletal and connective tissue, and nervous systems.
Most treatments for mps are symptomatic and cannot prevent the eventual decline in function. However, specific therapies, such as hematopoietic stem cell transplantation or enzyme replacement, may alter the natural history of these diseases.
Dr. Michael Ekizian
Dr. Michael Ekizian
Thank
Read more answers from doctors