6 doctors weighed in:

How can gene therapy help a cystic fibrosis sufferer?

6 doctors weighed in
Dr. HARRY OPSIMOS
Pediatrics - Pulmonology
3 doctors agree

In brief: Not available

There is currently no gene therapy available for cystic fibrosis (cf).
Since CF is a genetic disease, there is hope that, one day, gene therapy may provide a cure for this disease by, essentially, correcting the underlying genetic defect.

In brief: Not available

There is currently no gene therapy available for cystic fibrosis (cf).
Since CF is a genetic disease, there is hope that, one day, gene therapy may provide a cure for this disease by, essentially, correcting the underlying genetic defect.
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Dr. William Walsh
Addiction Medicine
1 doctor agrees

In brief: Direct effect

The new drug enables those with a subtype of CF to have a fully functioning sodium chloride transporter in the epithelium - and appears to stop the ill effects of the disease by doing so.

In brief: Direct effect

The new drug enables those with a subtype of CF to have a fully functioning sodium chloride transporter in the epithelium - and appears to stop the ill effects of the disease by doing so.
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