2 doctors weighed in:

Are leukodystrophies like metachromatic leukodystrophy (mld) treatable?

2 doctors weighed in
Dr. Colin Kerr
Family Medicine
1 doctor agrees

In brief: Leukodystrophy

There is no cure for mld.
Bone marrow transplantation may delay progression of the disease in some cases. Other treatment is symptomatic and supportive. Considerable progress has been made with regard to gene therapy in an animal model of mld. (http://www.Ninds.Nih.Gov/disorders/metachromatic_leukodystrophy/metachromatic_leukodystrophy.Htm).

In brief: Leukodystrophy

There is no cure for mld.
Bone marrow transplantation may delay progression of the disease in some cases. Other treatment is symptomatic and supportive. Considerable progress has been made with regard to gene therapy in an animal model of mld. (http://www.Ninds.Nih.Gov/disorders/metachromatic_leukodystrophy/metachromatic_leukodystrophy.Htm).
Dr. Colin Kerr
Dr. Colin Kerr
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