Related Questions

Is cell therapy different from gene therapy?

Yes. Cell therapy generally involves stem or pluripotent cells that have the potential, under the right triggers, to grow into many different types of cells. These cells are then transplanted to an area of disease. Gene therapy generally involves replacing small dysfunctional segments of dna. Dna is present in almost every cell in our body and is the instruction manual that tells the cell what to do. Read more...

What disease is gene therapy is used to treat?

Gene therapy. Treating certain congenital enzyme deficiency metabolic disorders. Looks promising in hemophilia where research going. Also lot of interest in cancers and treating infectious diseases. Read more...
Selected. Gene therapy describes an approach whereby genetic technology will be used to treat many conditions. The easiest use of gene therapy is to replace a faulty gene. An example is glybera which is approved in europe to treat lipoprotein lipase deficienct, a rare genetic disorder. Read more...

How should gene therapy treat certain diseases?

By replacing defect. Gene therapy is the use of genes for therapeutic effect. The original studies with gene therapy were for corrective gene therapy. To illustrate, patients with severe combined immunodefeciency were born with a mutation in the ada gene. The original gene therapy trial, engineered a virus that was used to infect bone marrow of children with this disorder. The normal gene corrected the disorder. Read more...