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Doctor insights on: Pros And Cons With Gene Therapy

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Pros of viral vectors in gene therapy?

Pros of viral vectors in gene therapy?

They work!: For gene therapy to work, material must be transported into cells, such as new genes to insert , or proteins that cleave (break apart) chains or delete genes. Since viruses are capable of entering cells (that is how they infect them) and are able to integrate their own genes into the dna inside the cell, they can be effective in gene therapy. But the virus must be or be made harmless first. ...Read more

Genetic (Definition)

From a medical standpoint, "genetic" refers to the potential heritability of various medical conditions. While some conditions are inevitable (at some point in one's life) as a consequence of simple genetic heritability (eg huntington's disease), a large number of medical conditions (including all behaviorial health disorders) are the expressed final pathway of a ...Read more


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What diseases can gene therapy help cure?

What diseases can gene therapy help cure?

Gene therapy: Here is some comprehensive information about gene therapy. http://ghr.nlm.nih.gov/handbook/therapy.pdf ...Read more

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Is cell therapy different from gene therapy?

Is cell therapy different from gene therapy?

Yes: Cell therapy generally involves stem or pluripotent cells that have the potential, under the right triggers, to grow into many different types of cells. These cells are then transplanted to an area of disease. Gene therapy generally involves replacing small dysfunctional segments of dna. Dna is present in almost every cell in our body and is the instruction manual that tells the cell what to do. ...Read more

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What are the complications with gene therapy?

What are the complications with gene therapy?

See: Here is some comprehensive information about gene therapy. http://ghr.nlm.nih.gov/handbook/therapy.pdf ...Read more

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How does gene therapy treat certain diseases?

How does gene therapy treat certain diseases?

Gene therapy: Here is some comprehensive information about gene therapy. http://ghr.nlm.nih.gov/handbook/therapy.pdf ...Read more

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What disease is gene therapy is used to treat?

What disease is gene therapy is used to treat?

Selected: Gene therapy describes an approach whereby genetic technology will be used to treat many conditions. The easiest use of gene therapy is to replace a faulty gene. An example is glybera which is approved in europe to treat lipoprotein lipase deficienct, a rare genetic disorder. ...Read more

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How much will gene therapy cost when available?

How much will gene therapy cost when available?

No one knows: It is not possible to know that. Gene therapy for any disease is likely a very technologically advanced therapy, so it is likely to be very expensive. Insurances should cover most, or some, of those therapies. The companies developing those therapies have a big say on this. ...Read more

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How should gene therapy treat certain diseases?

By replacing defect: Gene therapy is the use of genes for therapeutic effect. The original studies with gene therapy were for corrective gene therapy. To illustrate, patients with severe combined immunodefeciency were born with a mutation in the ada gene. The original gene therapy trial, engineered a virus that was used to infect bone marrow of children with this disorder. The normal gene corrected the disorder. ...Read more

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What are the two approaches to human gene therapy?

What are the two approaches to human gene therapy?

Gene therapy: Here is some comprehensive information about gene therapy. http://ghr.nlm.nih.gov/handbook/therapy.pdf ...Read more

Gene (Definition)

A hereditary unit consisting of a sequence of dna that occupies a specific location on a chromosome and determines a particular characteristic in an organism. Genes undergo mutation when their ...Read more


Dr. HARRY OPSIMOS
1,103 doctors shared insights

Gene Therapy (Definition)

Genes are the hereditary units of DNA. Gene therapy is a new area of research in which individuals with genetic diseases can be treated by the insertion, modification, or removal of ...Read more