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Doctor insights on: Gene Therapy For Albinism

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Why isn't gene therapy used to produce insulin?

Why isn't gene therapy used to produce insulin?

Gene therapy: A good question but no immediate answer.

I am confident that within the next 5-10 years there will be major advances to produce insulin in your body. Till then you have to be patient.

PS: There may be some ongoing clinical trials in which you could participate. ...Read more

Genetic (Definition)

From a medical standpoint, "genetic" refers to the potential heritability of various medical conditions. While some conditions are inevitable (at some point in one's life) as a consequence of simple genetic heritability (eg huntington's disease), a large number of medical conditions (including all behaviorial health disorders) are the expressed final pathway of a ...Read more


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Need expert help here. What are 3 benefits of gene therapy?

Need expert help here. What are 3 benefits of gene therapy?

Info: Here is some comprehensive information about gene therapy. Http://ghr. Nlm. Nih. Gov/handbook/therapy. Pdf ...Read more

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Is the gene therapy for aids?

Is the gene therapy for aids?

Gene therapy for HIV: Gene therapy for HIV could be coming. A company called sangamo pharm. Has developed a gene modification tool called a zinc-finger endonuclease that can alter on of the lymphocyte genes that allows HIV to enter the cells; called a chemokine receptor. They are involved in clinical studies at this time that look promising. ...Read more

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How does gene therapy cure diabetes?

How does gene therapy cure diabetes?

Possibly: I think the data is promising but not absolute. ...Read more

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Can you use gene therapy to treat cml?

Can you use gene therapy to treat cml?

No: "gene therapy" is not used as a treatment. However, the current treatments are designed to affect the genetic abnormality that leads to CML and are highly successful. ...Read more

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Pros of viral vectors in gene therapy?

They work!: For gene therapy to work, material must be transported into cells, such as new genes to insert, or proteins that cleave (break apart) chains or delete genes. Since viruses are capable of entering cells (that is how they infect them) and are able to integrate their own genes into the dna inside the cell, they can be effective in gene therapy. But the virus must be or be made harmless first. ...Read more

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Is gene therapy an option for Down syndrome?

Is gene therapy an option for Down syndrome?

No: Someone with Down syndrome has an entire extra chromosome 21, this is incorporated into every single cell in the entire body, and causes creation of abnormal cell proteins and function. You cannot just pull out an entire chromosome - we are nowhere near that type of genetic therapy yet. Focus instead on what wonderful, full-loving people those with that extra chromosome are and enjoy them! ...Read more

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Can gene therapy help with mitochondrial disorders?

Can gene therapy help with mitochondrial disorders?

Not yet: To date I have not heard of gene therapy applicable to mitochondrial disorders. ...Read more

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Can you tell me how gene therapy helps in curing various diseases?

Can you tell me how gene therapy helps in curing various diseases?

Gene therapy: Here is some comprehensive information about gene therapy. Http://ghr. Nlm. Nih. Gov/handbook/therapy. Pdf ...Read more

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Is there any research being done to start gene therapy for scheuermann disease?

Check this site: Not sure, but www. Clinicaltrials. Gov has information on any studies that would be looking into this. Look at this link: http://clinicaltrials. Gov/ct2/results? Term=calve+disease (i just put in calve disease as a search term, to get broader results). Good luck! ...Read more

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What are some of the major obstacles preventing the use of gene therapy in people?

What are some of the major obstacles preventing the use of gene therapy in people?

FDA approval: The biggest obstacle before the widespread use of gene therapy in the USA is obtaining FDA approval. A phase 3 trial is required prior to approval, treatment must show efficacy and minimal side effects compared to the disease being treated. Phase 3 trials have had problems with immune system rejection of the wrapping material/virus for the gene therapy as well as issues with dosing.. ...Read more

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Can you tell me how gene therapy would help to prevent inherited conditions and diseaeses?

Can you tell me how gene therapy would help to prevent inherited conditions and diseaeses?

Gene therapy: Here is some comprehensive information about gene therapy. Http://ghr. Nlm. Nih. Gov/handbook/therapy. Pdf ...Read more

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How do I know when will gene therapy become a reality for orphan diseases (single gene disorders)?

Glybera: The first gene therapy has now been approved in europe for an orphan disease. Several hundred therapies are currently in human clinical trials. So, I would say gene therapy is now a reality and the next 5 years will see a number of therapies approved. ...Read more

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What diseases can gene therapy help cure?

What diseases can gene therapy help cure?

Gene therapy: Here is some comprehensive information about gene therapy. Http://ghr. Nlm. Nih. Gov/handbook/therapy. Pdf ...Read more

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Is cell therapy different from gene therapy?

Yes: Cell therapy generally involves stem or pluripotent cells that have the potential, under the right triggers, to grow into many different types of cells. These cells are then transplanted to an area of disease. Gene therapy generally involves replacing small dysfunctional segments of dna. Dna is present in almost every cell in our body and is the instruction manual that tells the cell what to do. ...Read more

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What are the complications with gene therapy?

What are the complications with gene therapy?

See: Here is some comprehensive information about gene therapy. Http://ghr. Nlm. Nih. Gov/handbook/therapy. Pdf ...Read more

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How does gene therapy treat certain diseases?

How does gene therapy treat certain diseases?

Gene therapy: Here is some comprehensive information about gene therapy. Http://ghr. Nlm. Nih. Gov/handbook/therapy. Pdf ...Read more

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What disease is gene therapy is used to treat?

What disease is gene therapy is used to treat?

Selected: Gene therapy describes an approach whereby genetic technology will be used to treat many conditions. The easiest use of gene therapy is to replace a faulty gene. An example is glybera which is approved in europe to treat lipoprotein lipase deficienct, a rare genetic disorder. ...Read more

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How much will gene therapy cost when available?

How much will gene therapy cost when available?

No one knows: It is not possible to know that. Gene therapy for any disease is likely a very technologically advanced therapy, so it is likely to be very expensive. Insurances should cover most, or some, of those therapies. The companies developing those therapies have a big say on this. ...Read more

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How should gene therapy treat certain diseases?

By replacing defect: Gene therapy is the use of genes for therapeutic effect. The original studies with gene therapy were for corrective gene therapy. To illustrate, patients with severe combined immunodefeciency were born with a mutation in the ada gene. The original gene therapy trial, engineered a virus that was used to infect bone marrow of children with this disorder. The normal gene corrected the disorder. ...Read more

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What are the two approaches to human gene therapy?

What are the two approaches to human gene therapy?

Gene therapy: Here is some comprehensive information about gene therapy. Http://ghr. Nlm. Nih. Gov/handbook/therapy. Pdf ...Read more

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Could gene therapy occur before or after the baby's born?

Could gene therapy occur before or after the baby's born?

Gene therapy: Here is some comprehensive information about gene therapy. Http://ghr. Nlm. Nih. Gov/handbook/therapy. Pdf ...Read more

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Is it possible for an adult to grow healthier with gene therapy?

Is it possible for an adult to grow healthier with gene therapy?

Gene therapy: The problem with gene therapy is that the agent used to insert or remove a dysfunctionaal gene can alter dna in a way that could result in causing cancer. So far the most specific way to alter genes that has been deveolped is a zinc finger endonuclease (sangamo pharm.). They are studying ways to correct multiple types of abnormal genes that cause human diseases. ...Read more

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I'm curious as to how gene therapy has been used to treat disease?

Gene therapy: Here is some comprehensive information about gene therapy. Http://ghr. Nlm. Nih. Gov/handbook/therapy. Pdf ...Read more

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Can you tell me which are obstacles to use of gene therapy in medicine?

Can you tell me which are obstacles to use of gene therapy in medicine?

Gene therapy: Here is some comprehensive information about gene therapy. Http://ghr. Nlm. Nih. Gov/handbook/therapy. Pdf ...Read more

Gene (Definition)

A hereditary unit consisting of a sequence of dna that occupies a specific location on a chromosome and determines a particular characteristic in an organism. Genes undergo mutation when their dna sequence ...Read more


Dr. HARRY OPSIMOS
1,105 Doctors shared insights

Gene Therapy (Definition)

Genes are the hereditary units of DNA. Gene therapy is a new area of research in which individuals with genetic diseases can be treated by the insertion, modification, or removal of ...Read more